Design Therapeutics, Inc.

What Do They Do?

Develops small-molecule GeneTAC therapies for patients with inherited nucleotide repeat expansion diseases, including Friedreich ataxia, Fuchs endothelial corneal dystrophy, and myotonic dystrophy.

How Are They Changing?

Who Do They Compete With?

Competes with Biogen, Larimar Therapeutics, Lexeo Therapeutics, Minoryx Therapeutics, PTC Therapeutics, Solid Biosciences, Capsida Biotherapeutics, Papillon Therapeutics, Voyager Therapeutics, Aurion Biotech, Emmecell, Kowa Pharmaceutical, Santen Pharmaceutical, Trefoil Therapeutics, AMO Pharma, Arrowhead Pharmaceuticals, Arthex Biotech, Avidity Biosciences, Dyne Therapeutics, and EditForce