Develops nomlabofusp, a protein treatment designed to deliver frataxin to people with Friedreich’s ataxia, and uses its delivery platform to pursue treatments for other rare diseases.
10-K for FY2025, filed Mar 19, 2026
No revenue reported yet.
10-K, filed Mar 5, 2020
10-Q for Q2 FY2026, filed Aug 4, 2026
−$32.8MView ↗
Competes with Biogen, Design Therapeutics, Lexeo Therapeutics, Neurocrine Biosciences/Voyager Therapeutics, Solid Biosciences, and PTC Therapeutics
10-K for FY2025, filed Mar 19, 2026The biopharmaceutical industry is characterized by intense and dynamic competition to develop new technologies and proprietary therapies.…View ↗
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