Develops topical drug candidates for patients with rare skin diseases and vascular malformations, using its QTORIN platform to pursue treatments that act locally in the skin.
10-K for FY2025, filed Mar 31, 2026We are a clinical-stage biopharmaceutical company whose vision is to become the leading rare disease biopharmaceutical company focused on…View ↗
10-Q for Q2 FY2026, filed Aug 4, 2026
−$21.9MView ↗
From protein drugs to skin therapies
Moved from discovering and developing protein medicines across respiratory and cancer programs, with pharmaceutical-company collaborations, to developing topical treatments for rare skin diseases and vascular malformations.
10-K for FY2022, filed Mar 31, 2023 10-K for FY2025, filed Mar 31, 2026We are a clinical-stage biopharmaceutical company whose vision is to become the leading rare disease biopharmaceutical company focused on…View ↗
Competes with Kaken Pharmaceutical, Nobelpharma, Novartis Pharmaceuticals, Protara Therapeutics, Relay Therapeutics, Vaderis Therapeutics, and Quoin Pharmaceuticals
10-K for FY2025, filed Mar 31, 2026The pharmaceutical and biotechnology industries are characterized by rapidly advancing technologies, intense competition, and a strong…View ↗
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