2020 Q3 Form 10-Q Financial Statement

#000156459020047991 Filed on October 27, 2020

View on sec.gov

Income Statement

Concept 2020 Q3 2019 Q4 2019 Q3
Revenue $81.47M $35.59M $25.80M
YoY Change 215.78% 118.89% 119.33%
Cost Of Revenue $2.350M $5.110M $2.680M
YoY Change -12.31% 901.96% 881.68%
Gross Profit $79.12M $30.49M $23.12M
YoY Change 242.21% 93.59% 101.22%
Gross Profit Margin 97.12% 85.66% 89.61%
Selling, General & Admin $42.12M $41.88M $41.01M
YoY Change 2.72% 21.46% 31.87%
% of Gross Profit 53.24% 137.36% 177.36%
Research & Development $87.31M $83.06M $100.1M
YoY Change -12.81% 15.97% 42.98%
% of Gross Profit 110.36% 272.42% 433.15%
Depreciation & Amortization $3.090M $2.170M $2.140M
YoY Change 44.39% -26.19% -50.92%
% of Gross Profit 3.91% 7.12% 9.26%
Operating Expenses $131.8M $130.0M $143.8M
YoY Change -8.38% 21.99% 41.83%
Operating Profit -$50.32M -$99.56M -$118.0M
YoY Change -57.37% 9.58% 31.67%
Interest Expense -$10.18M $4.190M $5.490M
YoY Change -285.43% 59.32% 101.1%
% of Operating Profit
Other Income/Expense, Net $547.0K -$980.0K -$153.0K
YoY Change -457.52% -9900.0% 2.0%
Pretax Income -$68.53M -$91.24M -$112.7M
YoY Change -39.19% 4.04% 29.45%
Income Tax $313.0K $2.560M $290.0K
% Of Pretax Income
Net Earnings -$68.85M -$93.81M -$113.0M
YoY Change -39.07% 6.81% 29.42%
Net Earnings / Revenue -84.5% -263.55% -437.96%
Basic Earnings Per Share -$1.13
Diluted Earnings Per Share -$1.13 -$1.622M -$1.958M
COMMON SHARES
Basic Shares Outstanding
Diluted Shares Outstanding

Balance Sheet

Concept 2020 Q3 2019 Q4 2019 Q3
SHORT-TERM ASSETS
Cash & Short-Term Investments $765.5M $755.2M $527.1M
YoY Change 45.23% 64.29% 4.77%
Cash & Equivalents $197.5M $433.6M $122.6M
Short-Term Investments $568.0M $321.6M $404.5M
Other Short-Term Assets $64.20M $51.40M $49.20M
YoY Change 30.49% 19.81% -1.01%
Inventory $14.46M $11.55M $14.14M
Prepaid Expenses
Receivables $27.80M $32.84M $23.10M
Other Receivables $0.00 $0.00 $0.00
Total Short-Term Assets $872.0M $851.0M $613.5M
YoY Change 42.14% 62.91% 8.11%
LONG-TERM ASSETS
Property, Plant & Equipment $86.40M $44.35M $63.60M
YoY Change 35.85% 121.23% 221.21%
Goodwill $44.41M
YoY Change 0.0%
Intangibles $129.0M
YoY Change -0.17%
Long-Term Investments $129.3M $32.90M $26.30M
YoY Change 391.63%
Other Assets $5.092M $3.471M $3.100M
YoY Change 64.26% -1.22% -3.13%
Total Long-Term Assets $396.4M $284.5M $266.4M
YoY Change 48.79% 44.27% 34.82%
TOTAL ASSETS
Total Short-Term Assets $872.0M $851.0M $613.5M
Total Long-Term Assets $396.4M $284.5M $266.4M
Total Assets $1.268B $1.135B $879.9M
YoY Change 44.15% 57.8% 15.0%
SHORT-TERM LIABILITIES
YoY Change
Accounts Payable $10.85M $12.87M $13.50M
YoY Change -19.63% 4.86% 64.63%
Accrued Expenses $79.65M $83.19M $69.56M
YoY Change 14.51% 33.22% 18.9%
Deferred Revenue $102.9M $16.00K
YoY Change 643012.5%
Short-Term Debt $0.00 $0.00 $0.00
YoY Change
Long-Term Debt Due
YoY Change
Total Short-Term Liabilities $201.2M $103.3M $90.30M
YoY Change 122.81% 38.24% 35.38%
LONG-TERM LIABILITIES
Long-Term Debt $0.00 $0.00 $0.00
YoY Change
Other Long-Term Liabilities $367.7M $345.1M $31.20M
YoY Change 1078.53% 7151.52% 563.83%
Total Long-Term Liabilities $367.7M $345.1M $31.20M
YoY Change 1078.53% 7151.52% 563.83%
TOTAL LIABILITIES
Total Short-Term Liabilities $201.2M $103.3M $90.30M
Total Long-Term Liabilities $367.7M $345.1M $31.20M
Total Liabilities $602.2M $481.7M $152.7M
YoY Change 294.36% 335.37% 48.98%
SHAREHOLDERS EQUITY
Retained Earnings -$1.433B
YoY Change 39.09%
Common Stock $58.00K
YoY Change 13.73%
Preferred Stock
YoY Change
Treasury Stock (at cost)
YoY Change
Treasury Stock Shares
Shareholders Equity $666.2M $653.8M $727.3M
YoY Change
Total Liabilities & Shareholders Equity $1.268B $1.135B $879.9M
YoY Change 44.15% 57.8% 15.0%

Cashflow Statement

Concept 2020 Q3 2019 Q4 2019 Q3
OPERATING ACTIVITIES
Net Income -$68.85M -$93.81M -$113.0M
YoY Change -39.07% 6.81% 29.42%
Depreciation, Depletion And Amortization $3.090M $2.170M $2.140M
YoY Change 44.39% -26.19% -50.92%
Cash From Operating Activities -$61.97M -$72.04M -$88.50M
YoY Change -29.98% 28.97% 27.98%
INVESTING ACTIVITIES
Capital Expenditures -$6.050M -$11.50M -$5.030M
YoY Change 20.28% 858.33% 388.35%
Acquisitions
YoY Change
Other Investing Activities -$89.70M $78.76M $84.35M
YoY Change -206.34% 5.36% 389.27%
Cash From Investing Activities -$95.76M $67.27M $79.31M
YoY Change -220.74% -8.55% 389.27%
FINANCING ACTIVITIES
Cash Dividend Paid
YoY Change
Common Stock Issuance & Retirement, Net
YoY Change
Debt Paid & Issued, Net
YoY Change
Cash From Financing Activities 19.13M 315.4M 900.0K
YoY Change 2025.56% 2477.21% -96.4%
NET CHANGE
Cash From Operating Activities -61.97M -72.04M -88.50M
Cash From Investing Activities -95.76M 67.27M 79.31M
Cash From Financing Activities 19.13M 315.4M 900.0K
Net Change In Cash -138.6M 310.7M -8.290M
YoY Change 1571.89% 937.68% -70.31%
FREE CASH FLOW
Cash From Operating Activities -$61.97M -$72.04M -$88.50M
Capital Expenditures -$6.050M -$11.50M -$5.030M
Free Cash Flow -$55.92M -$60.54M -$83.47M
YoY Change -33.01% 10.76% 22.53%

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us-gaap Nature Of Operations
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<div style="align:left;"> <table border="0" cellpadding="0" cellspacing="0" style="border-collapse:collapse; width:100%;"> <tr> <td style="width:4.54%;white-space:nowrap" valign="top"> <p style="margin-bottom:0pt;margin-top:0pt;font-weight:bold;font-size:10pt;font-family:Times New Roman;font-style:normal;text-transform:none;font-variant: normal;"><span style="font-weight:bold;font-size:10pt;font-family:Times New Roman;font-style:normal;text-transform:none;font-variant: normal;">1.</span></p></td> <td valign="top"> <p style="margin-bottom:0pt;margin-top:0pt;font-weight:bold;font-style:normal;text-transform:none;font-variant: normal;font-family:Times New Roman;font-size:10pt;">Organization </p></td></tr></table></div> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">Ultragenyx Pharmaceutical Inc. (the Company) is a biopharmaceutical company incorporated in California on April 22, 2010. The Company subsequently reincorporated in the state of Delaware in June 2011.</p> <p style="margin-top:4pt;margin-bottom:0pt;text-indent:5%;color:#000000;font-family:Times New Roman;font-size:10pt;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">The Company is focused on the identification, acquisition, development, and commercialization of novel products for the treatment of serious rare and ultra-rare genetic diseases. The Company has four approved therapies. Crysvita<span style="font-weight:bold;">®</span> (burosumab) is approved in the United States by the U.S. Food and Drug Administration (FDA) and in Canada for the treatment of X-linked hypophosphatemia (XLH) in adult and pediatric patients one year of age and older, and has received European conditional marketing authorization for the treatment of XLH with radiographic evidence of bone disease in children one year of age and older and adolescents with growing skeletons. In October 2020, this authorization was expanded to include older adolescents and adults. In Brazil, Crysvita is approved for treatment of XLH in adult and pediatric patients one year of age and older. <span style="color:#000000;">Crysvita was approved by the FDA on June 18, 2020 for the treatment of FGF23-related hypophosphatemia in tumor-induced osteomalacia (TIO), associated with phosphaturic mesenchymal tumors that cannot be curatively resected or localized in adults and pediatric patients 2 years of age and older. </span></p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">The Company has also received FDA approval for Mepsevii™ (vestronidase alfa), the first medicine approved for the treatment of children and adults with mucopolysaccharidosis VII (MPS VII), also known as Sly syndrome. In the European Union and the United Kingdom, Mepsevii is approved under exceptional circumstances for patients of all ages for the treatment of non-neurological manifestations of MPS VII. In Brazil, Mepsevii is approved for the treatment of MPS VII for patients of all ages. </p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">Dojolvi, formerly known as UX007, was approved by FDA on June 30, 2020 for the treatment of pediatric and adult patients severely affected by long-chain fatty acid oxidation disorders (LC-FAOD). </p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">In addition to the approved treatments, the Company has two ongoing clinical development programs. DTX301 is an adeno-associated virus 8 (AAV8) gene therapy product candidate in development for the treatment of patients with ornithine transcarbamylase (OTC) deficiency, the most common urea cycle disorder; and DTX401 is an AAV8 gene therapy product candidate for the treatment of patients with glycogen storage disease type Ia (GSDIa). The Company operates as one reportable segment.</p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">The Company has sustained operating losses and expects such annual losses to continue over the next several years. The Company’s ultimate success depends on the outcome of its research and development and commercialization activities, for which it expects to incur additional losses in the future. Management recognizes that the Company will likely need to raise additional capital to fully implement its business plans. Through September 30, 2020, the Company has relied primarily on the proceeds from equity offerings and its sale of future royalties to finance its operations.</p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;color:#000000;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">The Company will likely raise additional capital through the issuance of equity, borrowings, or strategic alliances with partner companies. However, if such financing is not available at adequate levels, the Company would need to reevaluate its operating plans.</p>
us-gaap Use Of Estimates
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<p style="margin-bottom:0pt;margin-top:13pt;text-indent:0%;font-weight:bold;font-size:10pt;font-family:Times New Roman;font-style:normal;text-transform:none;font-variant: normal;">Use of Estimates </p> <p style="margin-bottom:0pt;margin-top:4pt;text-indent:4.54%;font-size:10pt;font-family:Times New Roman;font-weight:normal;font-style:normal;text-transform:none;font-variant: normal;">The accompanying consolidated financial statements have been prepared in accordance with GAAP. The preparation of the consolidated financial statements in conformity with GAAP requires management to make estimates and assumptions that affect the reported amounts of assets and liabilities, disclosure of contingent liabilities and the reported amounts of expenses in the consolidated financial statements and the accompanying notes. On an ongoing basis, management evaluates its estimates, including those related to clinical trial accruals, fair value of assets and liabilities, income taxes, stock-based compensation, and the liability related to the sale of future royalties. Management bases its estimates on historical experience and on various other market-specific and relevant assumptions that management believes to be reasonable under the circumstances. Actual results could differ from those estimates. </p>
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CY2020Q3 us-gaap Antidilutive Securities Excluded From Computation Of Earnings Per Share Amount
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